Solid Biosciences Advances Toward Transformative Genetic Medicines with Expanded Pipeline and New Clinical Milestones

17 January 2025 | Friday | News

The company highlights key developments in gene therapies for Duchenne muscular dystrophy, Friedreich's ataxia, and beyond, setting the stage for significant growth in 2025.
Picture Courtesy | Public Domain

Picture Courtesy | Public Domain

Solid Biosciences Inc. (Nasdaq: SLDB) (the “Company” or “Solid”), a life sciences company developing precision genetic medicines for neuromuscular and cardiac diseases, will provide a corporate update outlining the Company’s expanded clinical-stage pipeline and 2025 objectives as it completes its transformation into a multi-program leader in the development of precision genetic medicines. Bo Cumbo, President and CEO, and Gabriel Brooks, M.D., Chief Medical Officer, will provide the update at the 43rd Annual J.P. Morgan Healthcare Conference on Wednesday, January 15, 2025, at 3:45 p.m. PT (6:45 p.m. ET).

“At the time I joined Solid Biosciences there was a singular focus on genetic treatments for Duchenne muscular dystrophy,” said Bo Cumbo, President and CEO of Solid Biosciences. “In the last two years, we have broadened the pipeline to include gene therapy treatments for other devastating genetic neuromuscular and cardiac diseases, entered the clinic with our next generation gene therapy for Duchenne, opened a second IND with an industry first dual route of administration gene therapy to treat Friedreich’s ataxia, and continued to make advancements in next-generation capsid technologies, novel promoters, immunomodulation techniques, and manufacturing excellence. We are committed to innovating and building a true ‘next generation’ genetic medicines company, while maintaining Solid’s historic focus on the needs of the patient.”

He continued: “With two clinical stage assets and a third IND submission anticipated in 1H 2025, Solid Biosciences stands on the threshold of realizing that vision: a platform poised to create transformative genetic medicines for patients and create value for our shareholders.”

Survey Box

Poll of the Week

Which area of biopharmaceutical research excites you the most?

× Please select an option to participate in the poll.
Processing...
× You have successfully cast your vote.
 {{ optionDetail.option }}  {{ optionDetail.percentage }}%
 {{ optionDetail.percentage }}% Complete
More polls
Stay Connected

Sign up to our free newsletter and get the latest news sent direct to your inbox

© 2025 Biopharma Boardroom. All Rights Reserved.

Show

Forgot your password?

Show

Show

Lost your password? Please enter your email address. You will receive a link to create a new password.

Back to log-in

Close